Tag: rare disease patient access

Decentralized Clinical Trials in Rare Diseases: Opportunities and Risks

August 23, 2025

Decentralized Clinical Trials in Rare Diseases: Opportunities and Risks Harnessing Decentralized Clinical Trials to Improve Access in Rare Disease Research The Rationale for Decentralization in Rare Disease Trials Rare disease trials face one central challenge: patient scarcity scattered across vast geographies. Traditional site-based clinical trials often fail to recruit sufficient participants due to travel limitations,…

Rare and Orphan Disease Trials, Trial Design & Methodology

Strategies for Recruiting Rare Disease Patients Across Multiple Countries

August 1, 2025

digi

Strategies for Recruiting Rare Disease Patients Across Multiple Countries Effective Patient Recruitment Strategies for Multinational Rare Disease Trials The Need for Global Recruitment in Rare Disease Trials Given the inherently small and geographically dispersed populations affected by rare diseases, clinical trial sponsors often need to recruit participants from multiple countries to achieve statistically relevant sample…

Patient Recruitment Challenges, Rare and Orphan Disease Trials